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5 Facts you should know about

Niemann-Pick disease type A

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1

Type A is the most severe form.

2

It begins in early infancy and occurs most often in Jewish families.

3

Additional symptoms include weakness, an enlarged liver and spleen, swollen lymph nodes, and profound brain damage by six months of age.

4

Children with this type rarely live beyond 18 months.

5

Mutations in the SMPD1 gene cause Niemann–Pick disease type A.

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